Progress in anti-VEGF gene therapy for age-related macular degeneration

by DBGen Ocular Genomics

4 months ago
retina, vision, gene therapy, ADM, Regenxbio, Adverum Biotechnologies

Macular degeneration, Age-related macular degeneration, Gene Therapy

A new cancer immune therapy spin-off of Hospital Clínic-IDIBAPS (Barcelona) secures a 1.5 million-euro investment from Invivo Ventures

by Invivo Capital

5 months ago
Invivo Ventures, Gyala Therapeutics, Invivo Capital, gene therapy

Hospital Clínic – IDIBAPS (Barcelona) has founded Gyala Therapeutics, a new spin-off company focused on developing new CAR-T therapies for treating hematological malignancies. The company raised

Advances in gene therapy for retinitis pigmentosa due to RPGR gene mutation

by DBGen Ocular Genomics

6 months ago
Retinal Dystrophy, Retinitis pigmentosa, Gene Therapy

In the first months of 2020, positive results in gene therapy of X-linked retinitis pigmentosa (XLRP) have been reported. XLRP is an inherited genetic disorder that causes progressive vision loss, mai...

Researchers identify a fundamental protein to guarantee liver regeneration

by Universitat de Barcelona

6 months ago
protein, liver, transplant, gene therapy

Researchers from the Faculty of Medicine of the University of Barcelona and the CELLEX Biomedical Research Centre from IDIBAPS, in collaboration with scientists from the University of Sydney, Universi...

The Sant Pau Research Institute (IR Sant Pau) and the UAB create the Joint Research Unit in Genomic Medicine UAB – IR Sant Pau

by Hospital de la Santa Creu i Sant Pau

12 months ago
Genomic Medicine, diagnosis, pathophysiology, gene therapy

The Research Institute of the Hospital de la Santa Creu i Sant Pau and the Autonomous University of Barcelona have created the Joint Research Unit in Genomic Medicine UAB – IR Sant Pau with the aim ...

Stargardt’s disease: the research being conducted

by BMF Barcelona Macula Foundation: Research for Vision

1 year ago
Stargardt’s disease, young people, reduction of visual, Gene therapy, vitamin A, visual process, Human stem cells

There is still no treatment for Stargardt’s disease, which mainly affects young people. However, the research is highly intensive and encouraging

A gene therapy based clinical trial for Fanconi anemia patients offers its first successful results

by Universitat Autònoma de Barcelona (UAB)

1 year ago
gene therapy, anemia, cancer, Fanconi, Rocket Pharmaceuticals

A study, in which Dr. Jordi Surrallés, Professor of Genetics at the UAB, and his research group have participated, presents the first clinical demonstration of engraftment and expansion of gene-corre...

Luxturna: the first licensed gene therapy for rare inherited eye disorder is recommended by NICE

by Asphalion

1 year ago
inherited retinal dystrophy, eye, NICE, gene therapy

A draft NICE guidance recommends Voretigene Neparvovec (also called Luxturna) to treat people with vision loss caused by inherited retinal dystrophy from confirmed RPE65 gene mutations who have enough...

New gene therapy for autosomal dominant retinitis pigmentosa

by DBGen Ocular Genomics

1 year ago
gene therapy, retinitis, drug, dystrophy

The United States Food and Drug Administration (FDA) has just approved the designation of the QR-1123 therapy by the Dutch company ProQR as a new investigational drug. This drug aims to treat a form o...

The eyes: excellent candidates for stem cell therapies

by Fundació Clínic per a la Recerca Biomèdica

1 year ago
eyes, cell therapy, gene therapy, stem cells, regeneration of the cornea, implant cells

Replacing the cells of a damaged tissue with healthy ones using stem cells is now a reality.

CIC bioGUNE researchers decode new extremophile viruses whose assembly is related to human viruses

by CIC bioGUNE

2 years ago
gene therapy, virus, proteins, infeccions, microscopy

The researchers have studied two viruses which live in salt lakes and have an extraordinary survival capacity, and are crucial in understanding some of the viruses of today.

Asphalion attended CardioReGenix H2020 project kick-off meeting

by Asphalion

2 years ago
gene therapy, programme, CardioReGenix, heart disease, clinical care

The European Union has awarded a grant of 15€ million for a research programme – CardioReGenix – to support new gene therapy approaches for the treatment of heart disease.