Innovative gene therapy for autosomal dominant retinitis pigmentosa

by DBGen Ocular Genomics

2 years ago
Retinitis pigmentosa, Gene Therapy, Retinal Dystrophy

Mutations in the RHO gene are the main cause of dominant forms of retinitis pigmentosa (RP). RHO dictates the production of rhodopsin, a transmembrane protein present in large quantities in the outer ...

Novel high-precision gene therapy to correct an eye disease in mice

by DBGen Ocular Genomics

3 years ago
Gene Therapy, Gene editing

Researchers from the Seoul National University (Korea) have applied for the first an improved genome-editing methodology, named prime editing to correct the genetic defects of two animal models of hum...

Encouraging advances in therapies for Leber congenital amaurosis

by DBGen Ocular Genomics

3 years ago
CRISPR therapy, Leber congenital amaurosis, gene therapy

Editas Medicine, a company specialising in the development of gene editing therapies, has announced the recruitment of paediatric patients to the Brilliance trial.

Advanced gene therapy prevents 12-year-old girl from going blind

by Fundació Sant Joan de Déu

3 years ago
Luxturna therapy, gene therapy, Ophthalmology Department, hereditary retinal dystrophies

The SJD-Hospital Bellvitge Hereditary Retinal Dystrophy Unit has applied Novartis' Luxturna therapy to Noa, who only retained 3% of her vision.

Avoiding Costly IP Missteps: Insights for high-quality due diligence searches

by CAS, a division of the American Chemical Society

3 years ago
webinar, IP search, chemical, diligence searches, legal conflicts, oncology, gene therapy, life science

As chemical and life science companies seeking to monetize their IP portfolios emerge from the challenges of COVID-19, 2021 looks to be a year that will see increased product licensing, acquisitions a...

Sartorius Partners With RoosterBio to Advance Cell and Gene Therapy Manufacturing

by Sartorius Stedim Spain

3 years ago
stem cells, regenerative medicine, life science, Gene Therapy, RoosterBio

The life science company Sartorius signed a strategic collaboration with RoosterBio Inc., a leading supplier of human mesenchymal stem/stromal cell (hMSC) working cell banks, highly engineered media a...

A CNIO study links severe COVID-19 disease to short telomeres

by CNIO - Centro Nacional de Investigaciones Oncológicas

3 years ago
Covid-19, telomeres, regeneration, prolonged sequelae, pulmonary fibrosis, Gene therapy, aging

Patients with severe COVID-19 disease have significantly shorter telomeres, according to a study conducted by researchers at the Spanish National Cancer Research Centre (CNIO) in collaboration with th...

Christopher Mann – New Scientific and Regulatory Affairs Director

by Asphalion

3 years ago
muscular dystrophy, Christopher Mann, Biochemistry, gene therapy

Asphalion’s Board of Directors is pleased to announce the appointment of Christopher Mann as new Scientific and Regulatory Affairs Director.

Sartorius acquires filtration expert WaterSep BioSeparations

by Sartorius Stedim Spain

3 years ago
gene therapy, Sartorius, WaterSep BioSeparations, biopharmaceutical applications, cell therapy

The life science company Sartorius today acquired U.S.‑based purification expert WaterSep BioSeparations LLC through its subgroup Sartorius Stedim Biotech.

We interview Sara Secall, Inveready’s Director of Investments in Life Sciences

by GENESIS Biomed

3 years ago
Life Sciences, Inveready, Sara Secall, drugs, diagnosis, Health, gene therapy

Sara Secall, a chemistry graduate with a master’s degree in environmental science and an MBA, is the current partner and director of investments in Life Sciences at Inveready, a Venture Capital (VC)...

Progress in anti-VEGF gene therapy for age-related macular degeneration

by DBGen Ocular Genomics

4 years ago
retina, vision, gene therapy, ADM, Regenxbio, Adverum Biotechnologies

Macular degeneration, Age-related macular degeneration, Gene Therapy

A new cancer immune therapy spin-off of Hospital Clínic-IDIBAPS (Barcelona) secures a 1.5 million-euro investment from Invivo Ventures

by Invivo Capital

4 years ago
Invivo Ventures, Gyala Therapeutics, Invivo Capital, gene therapy

Hospital Clínic – IDIBAPS (Barcelona) has founded Gyala Therapeutics, a new spin-off company focused on developing new CAR-T therapies for treating hematological malignancies. The company raised