A natural compound designated as an orphan drug for cystinuria

by Hospital Universitari de Bellvitge

Cystinuria is a rare disease characterized by the formation of cystine stones in the kidney and urinary tract.

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Minoryx Therapeutics receives Orphan Drug Designation from the US FDA for its lead candidate MIN-102

by Professional Newco

MIN-102 targets X-linked Adrenoleukodystrophy (X-ALD), a life threatening orphan CNS disease with high unmet medical need. Orphan drug status for MIN-102 has now been granted by both the FDA and the E...

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