A study published today in the journal Cell marks the first reported instance of generative AI designing synthetic molecules that can successfully control gene expression in healthy mammalian cells. R...
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AAVion®, a fully integrated AAV manufacturing platform designed to accelerate gene therapy development. A ready-to-use Plasmid Platform intended to meet the increasing demand for plasmid DNA
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La Dra. Marta Guerra del grupo GEMAT lidera un proyecto innovador para desarrollar nuevos vectores virales recombinantes híbridos (rAAVs) y seleccionar los que ofrecen la mejor protección inmunitari...
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Joint achievement by Danaher operating companies highlights successful manufacture of world's first personalized CRISPR gene editing therapy for urea cycle disorder.
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It has been discovered new molecular mechanisms related to the cognitive decline associated with Alzheimer’s disease, the most common dementia. This study, carried out on animal models with the dise...
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Behind every scientific breakthrough and every patient receiving successful treatment, there’s a fundamental pillar, often invisible to the general public: the quality and safety of manufacturing fa...
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Esta terapia supone la recogida y purificación de las células madre de los pacientes, seguido de la corrección de su defecto genético, y finalmente la reinfusión de las células madre corregidas ...
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Una delegación de la Fundación AHUCE visita el instituto para conocer de cerca los avances del proyecto europeo MORBIUS, liderado por el Dr. Iván Durán y la Dra. Lidiia Zhytnik; en colaboración c...
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The funding will be used to advance the clinical development of SpliceBio’s lead gene therapy candidate, SB-007 for Stargardt disease, including the ongoing interventional Phase 1/2 ASTRA study and ...
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An international team of researchers has published results of a phase 2/3 clinical trial evaluating the efficacy and safety of leriglitazone, a new oral drug for the treatment of pediatric cerebral ad...
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The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to a new gene therapy for Amyotrophic Lateral Sclerosis (ALS) developed at the Universitat Autònoma de Barcelona and li...
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New purity offering, off-target analysis services and additional solutions help to bridge the gap from discovery research to clinical translation and advance CRISPR-based therapies
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La mejor actitud que podemos adoptar es la de trat...
The research team observed changes in head circumf...
AtCDF3 gene induced greater production of sugars a...
En nuestro post hablamos sobre este interesante tipo de célula del...
Telum Therapeutics, a biotechnology company leveraging proprietary met...
